Rapamycin, an anti-rejection drug for organ transplant patients, has now been shown to increases survival in and delayed symptoms of Leigh’s syndrome. The drug appears to cause a metabolic switch that bypasses the mitochondrial deficiency.
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In children with this form of leukemia, damage to chromosome 9 removes part of a normal copy of the gene in question, and leaves the mutated copy unopposed.
A trace substance in caramelized sugar, when purified and given in appropriate doses, improves muscle regeneration in insect and animal models of Duchenne muscular dystrophy.